Celebrating 30 Years of Rare

Our Rare Humanitarian Program, the first humanitarian initiative of its kind for people with lysosomal storage disorders and the longest running program of its kind, began in 1991 when our first treatment for Gaucher disease was approved by the U.S. FDA. For the past 30 years, the program has been focused on providing access to free treatments for patients who meet the program’s criteria, who otherwise would not have access to such treatments.

Through this interactive experience, explore first-hand stories from patients, families, physicians and partners. Their personal journeys of strength, determination, perseverance and hope help to define this program and inspire us to do more.

30 Years for Rare