Innovating in rare diseases
Life is a health journey that for some starts with being born with a rare genetic disorder. There are more than 7,000 rare diseases in the world, and 30% of children affected die before reaching their 5th birthday.
As a health journey partner,
Sanofi has been working on several rare diseases, including for example enzyme replacement therapy to treat Gaucher disease, considered an ultra-rare disease with fewer than 10,000 patients globally.