Our mission is to improve the lives of people everywhere through innovative vaccines and medicines. To do that, we apply new techniques to overcome barriers and accelerate progress. We never settle. Our deep expertise in disease pathways helps us take aim at smart targets, while our unique technologies empower us to develop drugs, biologics, and genomic medicines with the potential to transform the practice of medicine.
With deep expertise in immuno-oncology and molecular oncology, our R&D teams have doubled down on difficult-to-treat cancers of the breast, lung, and blood. Thanks to cutting-edge tools like AI, synthetic biology, NANOBODY® technology, and antibody–drug conjugates, our teams are developing powerful precision therapeutics, designed to meet the specific needs of patients.
Patient insights and outstanding science drive our development of new therapeutics for people with neurological disorders. Using revolutionary technologies, our teams are developing targeted, potentially disease-modifying therapies for people with multiple sclerosis (MS) and amyotrophic lateral sclerosis (ALS). The goal: to design best-in-class medicines that slow or halt neurodegeneration, control neuroinflammation, and protect or even repair the nervous system.
We’re proud of our legacy in lysosomal storage disorders: a group of rare, genetic conditions caused by enzyme deficiencies. Working closely with patient communities, we’ve been developing pioneering medicines for Fabry, Gaucher, and Pompe diseases, and advancing toward new treatments for patients with acid sphingomyelinase deficiency (ASMD) and GM2 gangliosidoses (Tay-Sachs disease, AB variant, and Sandhoff disease).